Gene therapy for muscular dystrophy: current progress and future prospects

Capucine Trollet, Takis Athanasopoulos, Linda Popplewell, Alberto Malerba, George Dickson

Research output: Contribution to journalLiterature reviewpeer-review

Original languageEnglish
Pages (from-to)849-866
Number of pages18
JournalExpert Opinion on Biological Therapy
Volume9
Issue number7
DOIs
Publication statusPublished - Jul 2009

Keywords

  • AAV
  • antisense therapy
  • clinical trial
  • gene replacement
  • gene therapy
  • lentivirus
  • muscular dystrophy
  • SKELETAL-MUSCLE MASS
  • MYOSTATIN PROPEPTIDE GENE
  • MDX MOUSE MUSCLE
  • MESSENGER-RNA
  • IN-VIVO
  • AUTOLOGOUS TRANSPLANTATION
  • STEM-CELLS
  • LIFE-SPAN
  • SATELLITE CELLS
  • ANTISENSE OLIGONUCLEOTIDES

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