Recombinant adeno-associated viral (rAAV) vectors as therapeutic tools for Duchenne muscular dystrophy (DMD)

T Athanasopoulos, I R Graham, H Foster, G Dickson

Research output: Contribution to journalArticlepeer-review

Original languageEnglish
Pages (from-to)S109-S121
Number of pages13
JournalHuman Gene Therapy
Volume11 Suppl 1
DOIs
Publication statusPublished - Oct 2004

Keywords

  • AAV
  • virus
  • microdystrophin
  • DMD
  • muscle
  • TRANSGENIC MDX MICE
  • MEDIATED GENE-TRANSFER
  • FULL-LENGTH DYSTROPHIN
  • CONTRACTION-INDUCED INJURY
  • NONHUMAN PRIMATE MUSCLE
  • VIRUS TYPE-2 VECTORS
  • LONG-TERM EXPRESSION
  • ACTIN-BINDING DOMAIN
  • SKELETAL-MUSCLE
  • FACTOR-IX

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